501 - 550 of 6422 Results
Title
Year
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OPENTitle: The small molecule alpha-synuclein misfolding inhibitor, NPT200-11, produces multiple benefits in an animal model of Parkinson’s diseaseJournal Name: Scientific ReportsPublisher: Springer Science and Business Media LLCVol: 8Issue #: 1Start Page:End Page:Publication Date:Open Access(OA) Status: OPENLicense: cc-byDOI - Digital Object Identifier: 10.1038/s41598-018-34490-9Best OA location URL: https://www.nature.com/articles/s41598-018-34490-9.pdfCitation Count: 143
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OPENTitle: Protein disulfide isomerase ERp57 protects early muscle denervation in experimental ALSJournal Name: Acta Neuropathologica CommunicationsPublisher: Springer Science and Business Media LLCVol: 9Issue #: 1Start Page:End Page:Publication Date:Open Access(OA) Status: OPENLicense: cc-byDOI - Digital Object Identifier: 10.1186/s40478-020-01116-zBest OA location URL: https://actaneurocomms.biomedcentral.com/track/pdf/10.1186/s40478-020-01116-zCitation Count: 16
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OPENTitle: Widespread transneuronal propagation of α-synucleinopathy triggered in olfactory bulb mimics prodromal Parkinson’s diseaseJournal Name: Journal of Experimental MedicinePublisher: Rockefeller University PressVol: 213Issue #: 9Start Page: 1759End Page: 1778Publication Date:Open Access(OA) Status: OPENLicense:DOI - Digital Object Identifier: 10.1084/jem.20160368Best OA location URL: http://doi.org/10.1084/jem.20160368Citation Count: 348
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OPENTitle: LRRK2 phosphorylates pre-synaptic N-ethylmaleimide sensitive fusion (NSF) protein enhancing its ATPase activity and SNARE complex disassembling rateJournal Name: Molecular NeurodegenerationPublisher: Springer Science and Business Media LLCVol: 11Issue #: 1Start Page:End Page:Publication Date:Open Access(OA) Status: OPENLicense: cc-byDOI - Digital Object Identifier: 10.1186/s13024-015-0066-zBest OA location URL: https://molecularneurodegeneration.biomedcentral.com/track/pdf/10.1186/s13024-015-0066-zCitation Count: 171
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OPENTitle: The Liquid State of RIM1α and RBP Condensates is Maintained by LipidsJournal Name: ACS NanoPublisher: American Chemical Society (ACS)Vol:Issue #:Start Page:End Page:Publication Date:Open Access(OA) Status: OPENLicense:DOI - Digital Object Identifier: 10.1021/acsnano.5c07661Best OA location URL: https://doi.org/10.1021/acsnano.5c07661Citation Count: 0
- Structural and Functional Characterization of the Most Frequent Pathogenic PRKN Substitution p.R275W2024OPENTitle: Structural and Functional Characterization of the Most Frequent Pathogenic PRKN Substitution p.R275WJournal Name: CellsPublisher: MDPI AGVol: 13Issue #: 18Start Page: 1540End Page: 1540Publication Date:Open Access(OA) Status: OPENLicense: cc-byDOI - Digital Object Identifier: 10.3390/cells13181540Best OA location URL: https://doi.org/10.3390/cells13181540Citation Count: 2
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OPENTitle: Structural and Functional Impact of Parkinson Disease-Associated Mutations in the E3 Ubiquitin Ligase ParkinJournal Name: Human MutationPublisher: WileyVol: 36Issue #: 8Start Page: 774End Page: 786Publication Date:Open Access(OA) Status: OPENLicense:DOI - Digital Object Identifier: 10.1002/humu.22808Citation Count: 85
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OPENTitle: Motor subtype changes in early Parkinson's diseaseJournal Name: Parkinsonism & Related DisordersPublisher: Elsevier BVVol: 43Issue #:Start Page: 67End Page: 72Publication Date:Open Access(OA) Status: OPENLicense:DOI - Digital Object Identifier: 10.1016/j.parkreldis.2017.07.018Best OA location URL: http://doi.org/10.1016/j.parkreldis.2017.07.018Citation Count: 66
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OPENTitle: Left Prefrontal Connectivity Links Subthalamic Stimulation with Depressive SymptomsJournal Name: Annals of NeurologyPublisher: WileyVol: 87Issue #: 6Start Page: 962End Page: 975Publication Date:Open Access(OA) Status: OPENLicense: cc-by-nc-ndDOI - Digital Object Identifier: 10.1002/ana.25734Best OA location URL: https://doi.org/10.1002/ana.25734Citation Count: 101
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OPENTitle: Potential sources of interference with the highly sensitive detection and quantification of alpha‐synuclein seeds by qRT‐QuICJournal Name: FEBS Open BioPublisher: WileyVol: 10Issue #: 5Start Page: 883End Page: 893Publication Date:Open Access(OA) Status: OPENLicense: cc-byDOI - Digital Object Identifier: 10.1002/2211-5463.12844Best OA location URL: https://onlinelibrary.wiley.com/doi/pdfdirect/10.1002/2211-5463.12844Citation Count: 9
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OPENTitle: A prospective controlled study of a wearable rhythmic vibrotactile device for tremor in Parkinson’s diseaseJournal Name: Clinical NeurophysiologyPublisher: Elsevier BVVol: 172Issue #:Start Page: 51End Page: 60Publication Date:Open Access(OA) Status: OPENLicense: cc-byDOI - Digital Object Identifier: 10.1016/j.clinph.2025.02.255Best OA location URL: https://doi.org/10.1016/j.clinph.2025.02.255Citation Count: 3
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OPENTitle: The Genetic Landscape of Hereditary Spastic Paraplegia in GreeceJournal Name: Clinical GeneticsPublisher: WileyVol:Issue #:Start Page:End Page:Publication Date:Open Access(OA) Status: OPENLicense:DOI - Digital Object Identifier: 10.1111/cge.70113Best OA location URL: https://onlinelibrary.wiley.com/doi/pdfdirect/10.1111/cge.70113Citation Count: 0
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OPENTitle: Manual segmentation of the fornix, fimbria, and alveus on high-resolution 3T MRI: Application via fully-automated mapping of the human memory circuit white and grey matter in healthy and pathological agingJournal Name: NeuroImagePublisher: Elsevier BVVol: 170Issue #:Start Page: 132End Page: 150Publication Date:Open Access(OA) Status: OPENLicense:DOI - Digital Object Identifier: 10.1016/j.neuroimage.2016.10.027Citation Count: 74
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OPENTitle: Dopamine receptor D3 signalling in astrocytes promotes neuroinflammationJournal Name: Journal of NeuroinflammationPublisher: Springer Science and Business Media LLCVol: 16Issue #: 1Start Page:End Page:Publication Date:Open Access(OA) Status: OPENLicense: cc-byDOI - Digital Object Identifier: 10.1186/s12974-019-1652-8Best OA location URL: https://jneuroinflammation.biomedcentral.com/track/pdf/10.1186/s12974-019-1652-8Citation Count: 69
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OPENTitle: An estimate of the total number of true human miRNAsJournal Name: Nucleic Acids ResearchPublisher: Oxford University Press (OUP)Vol: 47Issue #: 7Start Page: 3353End Page: 3364Publication Date:Open Access(OA) Status: OPENLicense: cc-by-ncDOI - Digital Object Identifier: 10.1093/nar/gkz097Best OA location URL: https://academic.oup.com/nar/article-pdf/47/7/3353/28467549/gkz097.pdfCitation Count: 494
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OPENTitle: Toward a standard model for autophagosome biogenesisJournal Name: Journal of Cell BiologyPublisher: Rockefeller University PressVol: 222Issue #: 7Start Page:End Page:Publication Date:Open Access(OA) Status: OPENLicense: cc-by-nc-sa, cc-by-nc-saDOI - Digital Object Identifier: 10.1083/jcb.202304011Best OA location URL: https://escholarship.org/uc/item/8592h4hnCitation Count: 19
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OPENTitle: Post hoc analysis of the Exenatide‐ PD trial—Factors that predict responseJournal Name: European Journal of NeurosciencePublisher: WileyVol: 49Issue #: 3Start Page: 410End Page: 421Publication Date:Open Access(OA) Status: OPENLicense:DOI - Digital Object Identifier: 10.1111/ejn.14096Citation Count: 63
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OPENTitle: Rapid ex vivo reverse genetics identifies the essential determinants of prion protein toxicityJournal Name: Brain PathologyPublisher: WileyVol: 33Issue #: 2Start Page:End Page:Publication Date:Open Access(OA) Status: OPENLicense: cc-by-nc-ndDOI - Digital Object Identifier: 10.1111/bpa.13130Best OA location URL: https://onlinelibrary.wiley.com/doi/pdfdirect/10.1111/bpa.13130Citation Count: 4
- Mitoguardin-2–mediated lipid transfer preserves mitochondrial morphology and lipid droplet formation2022OPENTitle: Mitoguardin-2–mediated lipid transfer preserves mitochondrial morphology and lipid droplet formationJournal Name: Journal of Cell BiologyPublisher: Rockefeller University PressVol: 221Issue #: 12Start Page:End Page:Publication Date:Open Access(OA) Status: OPENLicense: cc-by, cc-byDOI - Digital Object Identifier: 10.1083/jcb.202207022Best OA location URL: https://doi.org/10.1083/jcb.202207022Citation Count: 36
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OPENTitle: Concurrent Validity of Zeno Instrumented Walkway and Video-Based Gait Features in Adults With Parkinson’s DiseaseJournal Name: IEEE Journal of Translational Engineering in Health and MedicinePublisher: Institute of Electrical and Electronics Engineers (IEEE)Vol: 10Issue #:Start Page: 1End Page: 11Publication Date:Open Access(OA) Status: OPENLicense: cc-byDOI - Digital Object Identifier: 10.1109/jtehm.2022.3180231Best OA location URL: https://ieeexplore.ieee.org/ielx7/6221039/6563131/09787410.pdfCitation Count: 26
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OPENTitle: Interplay between tau and α‐synuclein liquid–liquid phase separationJournal Name: Protein SciencePublisher: WileyVol: 30Issue #: 7Start Page: 1326End Page: 1336Publication Date:Open Access(OA) Status: OPENLicense: cc-by-ncDOI - Digital Object Identifier: 10.1002/pro.4025Best OA location URL: https://onlinelibrary.wiley.com/doi/pdfdirect/10.1002/pro.4025Citation Count: 83
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OPENTitle: Functional alterations in resting‐state networks for Theory of Mind in Parkinson's diseaseJournal Name: European Journal of NeurosciencePublisher: WileyVol: 59Issue #: 6Start Page: 1213End Page: 1226Publication Date:Open Access(OA) Status: OPENLicense: cc-byDOI - Digital Object Identifier: 10.1111/ejn.16145Best OA location URL: https://doi.org/10.1111/ejn.16145Citation Count: 2
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OPENTitle: Neurofilament Light Chain as a Biomarker for Cognitive Decline in Parkinson DiseaseJournal Name: Movement DisordersPublisher: WileyVol: 36Issue #: 12Start Page: 2945End Page: 2950Publication Date:Open Access(OA) Status: OPENLicense:DOI - Digital Object Identifier: 10.1002/mds.28779Best OA location URL: https://www.ncbi.nlm.nih.gov/pmc/articles/8688198Citation Count: 152
- α-Synuclein fibril-induced paradoxical structural and functional defects in hippocampal neurons2018OPENTitle: α-Synuclein fibril-induced paradoxical structural and functional defects in hippocampal neuronsJournal Name: Acta Neuropathologica CommunicationsPublisher: Springer Science and Business Media LLCVol: 6Issue #: 1Start Page:End Page:Publication Date:Open Access(OA) Status: OPENLicense: cc-by, cc-byDOI - Digital Object Identifier: 10.1186/s40478-018-0537-xBest OA location URL: https://actaneurocomms.biomedcentral.com/track/pdf/10.1186/s40478-018-0537-xCitation Count: 83
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OPENTitle: Network spreading and local biological vulnerability in amyotrophic lateral sclerosisJournal Name: Communications BiologyPublisher: Springer Science and Business Media LLCVol: 8Issue #: 1Start Page:End Page:Publication Date:Open Access(OA) Status: OPENLicense: cc-byDOI - Digital Object Identifier: 10.1038/s42003-025-08561-3Best OA location URL: https://www.nature.com/articles/s42003-025-08561-3.pdfCitation Count: 0
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OPENTitle: The vermiform appendix impacts the risk of developing Parkinson’s diseaseJournal Name: Science Translational MedicinePublisher: American Association for the Advancement of Science (AAAS)Vol: 10Issue #: 465Start Page:End Page:Publication Date:Open Access(OA) Status: OPENLicense:DOI - Digital Object Identifier: 10.1126/scitranslmed.aar5280Best OA location URL: https://hal.science/hal-04247698Citation Count: 249
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OPENTitle: Differential Effects of Pathological Beta Burst Dynamics Between Parkinson’s Disease Phenotypes Across Different MovementsJournal Name: Frontiers in NeurosciencePublisher: Frontiers Media SAVol: 15Issue #:Start Page:End Page:Publication Date:Open Access(OA) Status: OPENLicense: cc-byDOI - Digital Object Identifier: 10.3389/fnins.2021.733203Best OA location URL: https://www.frontiersin.org/articles/10.3389/fnins.2021.733203/pdfCitation Count: 26
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OPENTitle: Radioligands Targeting the Purinergic P2X ReceptorsJournal Name: CellsPublisher: MDPI AGVol: 14Issue #: 13Start Page: 984End Page: 984Publication Date:Open Access(OA) Status: OPENLicense: cc-byDOI - Digital Object Identifier: 10.3390/cells14130984Best OA location URL: https://www.mdpi.com/2073-4409/14/13/984/pdf?version=1751010309Citation Count: 0
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OPENTitle: In vivo detection of substantia nigra and locus coeruleus volume loss in Parkinson’s disease using neuromelanin-sensitive MRI: Replication in two cohortsJournal Name: PLOS ONEPublisher: Public Library of Science (PLoS)Vol: 18Issue #: 4Start Page: e0282684End Page: e0282684Publication Date:Open Access(OA) Status: OPENLicense: cc-byDOI - Digital Object Identifier: 10.1371/journal.pone.0282684Best OA location URL: https://journals.plos.org/plosone/article/file?id=10.1371/journal.pone.0282684&type=printableCitation Count: 14
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OPENTitle: Distinct AQP4 Alterations in Movement Disorders with Primary SynucleinopathyJournal Name: Movement DisordersPublisher: WileyVol:Issue #:Start Page:End Page:Publication Date:Open Access(OA) Status: OPENLicense: cc-by-nc-ndDOI - Digital Object Identifier: 10.1002/mds.70023Best OA location URL: https://onlinelibrary.wiley.com/doi/pdfdirect/10.1002/mds.70023Citation Count: 0
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OPENTitle: Genome-Wide Association Study of Glucocerebrosidase Activity ModifiersJournal Name: Molecular NeurobiologyPublisher: Springer Science and Business Media LLCVol: 62Issue #: 9Start Page:End Page:Publication Date:Open Access(OA) Status: OPENLicense: cc-byDOI - Digital Object Identifier: 10.1007/s12035-025-04996-1Best OA location URL: https://link.springer.com/content/pdf/10.1007/s12035-025-04996-1.pdfCitation Count: 0
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OPENTitle: Plasma pTau181 Reveals a Pathological Signature that Predicts Cognitive Outcomes in Lewy Body DiseaseJournal Name: Annals of NeurologyPublisher: WileyVol: 96Issue #: 3Start Page: 526End Page: 538Publication Date:Open Access(OA) Status: OPENLicense: cc-by-nc-ndDOI - Digital Object Identifier: 10.1002/ana.27003Best OA location URL: https://onlinelibrary.wiley.com/doi/pdfdirect/10.1002/ana.27003Citation Count: 5
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OPENTitle: Rational design of structure‐based vaccines targeting misfolded alpha‐synuclein conformers of Parkinson's disease and related disordersJournal Name: Bioengineering & Translational MedicinePublisher: WileyVol: 9Issue #: 4Start Page: e10665End Page: e10665Publication Date:Open Access(OA) Status: OPENLicense: cc-byDOI - Digital Object Identifier: 10.1002/btm2.10665Best OA location URL: https://onlinelibrary.wiley.com/doi/pdfdirect/10.1002/btm2.10665Citation Count: 2
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OPENTitle: Parkinson’s Disease Recognition Using SPECT Image and Interpretable AI: A TutorialJournal Name: IEEE Sensors JournalPublisher: Institute of Electrical and Electronics Engineers (IEEE)Vol: 21Issue #: 20Start Page: 22304End Page: 22316Publication Date:Open Access(OA) Status: OPENLicense:DOI - Digital Object Identifier: 10.1109/jsen.2021.3077949Best OA location URL: https://arxiv.org/pdf/1908.11199Citation Count: 29
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OPENTitle: scNAT: a deep learning method for integrating paired single-cell RNA and T cell receptor sequencing profilesJournal Name: Genome BiologyPublisher: Springer Science and Business Media LLCVol: 24Issue #: 1Start Page:End Page:Publication Date:Open Access(OA) Status: OPENLicense: cc-by, cc-byDOI - Digital Object Identifier: 10.1186/s13059-023-03129-yBest OA location URL: https://genomebiology.biomedcentral.com/counter/pdf/10.1186/s13059-023-03129-yCitation Count: 9
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OPENTitle: Fine‐Mapping of SNCA in Rapid Eye Movement Sleep Behavior Disorder and Overt SynucleinopathiesJournal Name: Annals of NeurologyPublisher: WileyVol: 87Issue #: 4Start Page: 584End Page: 598Publication Date:Open Access(OA) Status: OPENLicense:DOI - Digital Object Identifier: 10.1002/ana.25687Best OA location URL: http://hdl.handle.net/11380/1205937Citation Count: 57
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OPENTitle: Clinimetric Analysis of the Motor Section of the Progressive Supranuclear Palsy Rating Scale: Reliability and Factor AnalysisJournal Name: Movement Disorders Clinical PracticePublisher: WileyVol: 3Issue #: 1Start Page: 65End Page: 67Publication Date:Open Access(OA) Status: OPENLicense:DOI - Digital Object Identifier: 10.1002/mdc3.12243Best OA location URL: https://onlinelibrary.wiley.com/doi/pdfdirect/10.1002/mdc3.12243Citation Count: 9
- The REM Sleep Behavior Disorder Screening Questionnaire is not Valid in De Novo Parkinson's Disease2018OPENTitle: The REM Sleep Behavior Disorder Screening Questionnaire is not Valid in De Novo Parkinson's DiseaseJournal Name: Movement Disorders Clinical PracticePublisher: WileyVol: 5Issue #: 2Start Page: 171End Page: 176Publication Date:Open Access(OA) Status: OPENLicense: cc-byDOI - Digital Object Identifier: 10.1002/mdc3.12591Best OA location URL: https://onlinelibrary.wiley.com/doi/pdfdirect/10.1002/mdc3.12591Citation Count: 58
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OPENTitle: Radiolabeled Aminopyrazoles as Novel Isoform Selective Probes for pJNK3 QuantificationJournal Name: ACS Medicinal Chemistry LettersPublisher: American Chemical Society (ACS)Vol: 13Issue #: 10Start Page: 1606End Page: 1614Publication Date:Open Access(OA) Status: OPENLicense:DOI - Digital Object Identifier: 10.1021/acsmedchemlett.2c00278Best OA location URL: https://www.ncbi.nlm.nih.gov/pmc/articles/9575163Citation Count: 4
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OPENTitle: Deep-learning segmentation of the substantia nigra from multiparametric MRI: Application to Parkinson’s diseaseJournal Name: Imaging NeurosciencePublisher: MIT PressVol: 3Issue #:Start Page:End Page:Publication Date:Open Access(OA) Status: OPENLicense: cc-byDOI - Digital Object Identifier: 10.1162/imag.a.158Best OA location URL: https://direct.mit.edu/imag/article-pdf/doi/10.1162/IMAG.a.158/2551560/imag.a.158.pdfCitation Count: 0
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OPENTitle: Validation of a data-driven motion-compensated PET brain image reconstruction algorithm in clinical patients using four radiotracersJournal Name: EJNMMI PhysicsPublisher: Springer Science and Business Media LLCVol: 12Issue #: 1Start Page:End Page:Publication Date:Open Access(OA) Status: OPENLicense: cc-by-nc-ndDOI - Digital Object Identifier: 10.1186/s40658-025-00723-wBest OA location URL: https://link.springer.com/content/pdf/10.1186/s40658-025-00723-w.pdfCitation Count: 0
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OPENTitle: Generation of RAB39B knockout isogenic human embryonic stem cell lines to model RAB39B-mediated Parkinson's diseaseJournal Name: Stem Cell ResearchPublisher: Elsevier BVVol: 28Issue #:Start Page: 161End Page: 164Publication Date:Open Access(OA) Status: OPENLicense: cc-by-nc-ndDOI - Digital Object Identifier: 10.1016/j.scr.2018.02.015Best OA location URL: https://doi.org/10.1016/j.scr.2018.02.015Citation Count: 9
- Multiclass prediction of different dementia syndromes based on multi-centric volumetric MRI imaging2023OPENTitle: Multiclass prediction of different dementia syndromes based on multi-centric volumetric MRI imagingJournal Name: NeuroImage: ClinicalPublisher: Elsevier BVVol: 37Issue #:Start Page: 103320End Page: 103320Publication Date:Open Access(OA) Status: OPENLicense: cc-by-nc-ndDOI - Digital Object Identifier: 10.1016/j.nicl.2023.103320Best OA location URL: https://doi.org/10.1016/j.nicl.2023.103320Citation Count: 14
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OPENTitle: Inhibition of autophagic flux by S-nitrosylation of SQSTM1/p62 promotes neuronal secretion and cell-to-cell transmission of SNCA/α-synuclein in Parkinson disease and Lewy body dementiaJournal Name: Autophagy ReportsPublisher: Informa UK LimitedVol: 1Issue #: 1Start Page: 223End Page: 225Publication Date:Open Access(OA) Status: OPENLicense: cc-byDOI - Digital Object Identifier: 10.1080/27694127.2022.2076770Best OA location URL: https://www.tandfonline.com/doi/pdf/10.1080/27694127.2022.2076770?needAccess=trueCitation Count: 6
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OPENTitle: Chronotype, sleep, and sleepiness in Parkinson's diseaseJournal Name: Parkinsonism & Related DisordersPublisher: Elsevier BVVol: 106Issue #:Start Page: 105189End Page: 105189Publication Date:Open Access(OA) Status: OPENLicense: other-oaDOI - Digital Object Identifier: 10.1016/j.parkreldis.2022.10.011Best OA location URL: https://doi.org/10.1016/j.parkreldis.2022.10.011Citation Count: 8
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OPENTitle: Differential protein–protein interactions of LRRK1 and LRRK2 indicate roles in distinct cellular signaling pathwaysJournal Name: Journal of NeurochemistryPublisher: WileyVol: 131Issue #: 2Start Page: 239End Page: 250Publication Date:Open Access(OA) Status: OPENLicense:DOI - Digital Object Identifier: 10.1111/jnc.12798Best OA location URL: https://onlinelibrary.wiley.com/doi/pdfdirect/10.1111/jnc.12798?download=trueCitation Count: 51
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OPENTitle: Cerebellar Volume and Disease Staging in Parkinson's Disease: An ENIGMA‐PD StudyJournal Name: Movement DisordersPublisher: WileyVol: 38Issue #: 12Start Page: 2269End Page: 2281Publication Date:Open Access(OA) Status: OPENLicense: other-oaDOI - Digital Object Identifier: 10.1002/mds.29611Best OA location URL: https://onlinelibrary.wiley.com/doi/pdfdirect/10.1002/mds.29611Citation Count: 12
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OPENTitle: Topological influence of immediate-early genes in brain genetic networks and their link to Alzheimer's diseaseJournal Name: Computers in Biology and MedicinePublisher: Elsevier BVVol: 190Issue #:Start Page: 110043End Page: 110043Publication Date:Open Access(OA) Status: OPENLicense:DOI - Digital Object Identifier: 10.1016/j.compbiomed.2025.110043Best OA location URL: https://doi.org/10.1016/j.compbiomed.2025.110043Citation Count: 0
- X‐Chromosome Association Study in Latin American Cohorts Identifies New Loci in Parkinson's Disease2023OPENTitle: X‐Chromosome Association Study in Latin American Cohorts Identifies New Loci in Parkinson's DiseaseJournal Name: Movement DisordersPublisher: WileyVol: 38Issue #: 9Start Page: 1625End Page: 1635Publication Date:Open Access(OA) Status: OPENLicense: cc-by-nc-ndDOI - Digital Object Identifier: 10.1002/mds.29508Best OA location URL: https://onlinelibrary.wiley.com/doi/pdfdirect/10.1002/mds.29508Citation Count: 16
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OPENTitle: RETRACTED: Development of Nonviral Vectors Targeting the Brain as a Therapeutic Approach For Parkinson's Disease and Other Brain DisordersJournal Name: Molecular TherapyPublisher: Elsevier BVVol: 24Issue #: 4Start Page: 746End Page: 758Publication Date:Open Access(OA) Status: OPENLicense:DOI - Digital Object Identifier: 10.1038/mt.2015.232Best OA location URL: http://www.cell.com/article/S1525001616309984/pdfCitation Count: 40